Email this article Gene Therapy for Rare Genetic Diseases
- Authors: Lundstrom K.1, Yannaki E.2, Chou J.3, Saad F.4
-
Affiliations:
- , Pan Therapeutics
- Hematology Department, Hematopoietic Cell Transplantation Unit,, Gene and Cell Therapy Center, George Papanikolaou Hospital
- Section on Cellular Differentiation, Division of Translational Medicine, Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health
- Department of Gene Therapy, Saad Pharmaceuticals
- Issue: Vol 24, No 1 (2024)
- Pages: 4-5
- Section: Life Sciences
- URL: https://j-morphology.com/1566-5232/article/view/643895
- DOI: https://doi.org/10.2174/1566523223666230320120839
- ID: 643895
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About the authors
Kenneth Lundstrom
, Pan Therapeutics
Email: info@benthamscience.net
Evangelia Yannaki
Hematology Department, Hematopoietic Cell Transplantation Unit,, Gene and Cell Therapy Center, George Papanikolaou Hospital
Email: info@benthamscience.net
Janice Chou
Section on Cellular Differentiation, Division of Translational Medicine, Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health
Email: info@benthamscience.net
Fawzy Saad
Department of Gene Therapy, Saad Pharmaceuticals
Author for correspondence.
Email: info@benthamscience.net
References
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- Saad FA, Saad JF, Siciliano G, Merlini L, Angelini C. Duchenne muscular dystrophy gene therapy. Current Gene Therapy In press
- Chou JY, Mansfield BC. Gene therapy for type I glycogen storage diseases. Current Gene Therapy 2007; 7(2): 79-88.
- Psatha N, Georgakopoulou A, Li C, et al. Enhanced HbF reactivation by multiplex mutagenesis of thalassemic CD34+ cells in vitro and in vivo. Blood 2021; 138(17): 1540-53.
- Kloess S, Kretschmer A, Stahl L, Fricke S, Koehl U. CAR-expressing natural killer cells for cancer retargeting. Transfus Med Hemother 2019; 46(1): 4-13.
- Li Y, Chen J, Tsai SQ, Cheng Y. Easy-Prime: A machine learning-based prime editor design tool. Genome Biol 2021; 22(1): 235.
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